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Gene Therapy & Genomic Medicine
CRISPR edits, delivery vectors, rare‑disease trials, and approvals.
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Latest in Gene Therapy & Genomic Medicine
Serbian Biotech Startup Takes Its Journey from Belgrade to Cambridge with Documentary on Longevity Science
11+ hour, 23+ min ago (116+ words) PA Media LifeSpan Vision Ventures Makes 7th Investment in Pursuit of Longevity Mission Kimera® Labs Named Semifinalist in $101 Million XPRIZE Healthspan Competition for Pioneering Innovations in Healthy Aging Seragon Completes Pre-Clinical Study of Aging Intervention Candidate SRN-901 Fifteen Years Alongside Europe's…...
Russian scientists create world???s first registered CRISPR/Cas test for antibiotic resistance | News
8+ hour, 30+ min ago (217+ words) Russian scientists create world’s first registered CRISPR/Cas test for antibiotic resistance Новости GxP Specialists at the Central Research Institute of Epidemiology of Rospotrebnadzor have developed a PCR test for determining antibiotic resistance, the agency’s press service reported. It is…...
Beacon's XLRP gene therapy meets pivotal U.S. endpoint - European Biotechnology Magazine
6+ hour, 54+ min ago (475+ words) Beacon Therapeutics' gene therapy laru-zova met its U.S. pivotal endpoint in X-linked retinitis pigmentosa, while results on the trial's separately designated European primary efficacy measure were less clear-cut. Why it matters: X-linked retinitis pigmentosa (XLRP) mainly affects boys and men, and…...
Andelyn Curator Biomanufacturing Platform Supports Fayuvi Gene Therapy Approval
3+ hour, 32+ min ago (267+ words) Sanfilippo syndrome type A (MPS IIIA) is a rare, fatal lysosomal storage disease that primarily affects the central nervous system and is marked by rapid neurodegeneration beginning in early childhood. The post Andelyn Curator Biomanufacturing Platform Supports Fayuvi Gene Therapy…...
Clayface Trailer Exposes CRISPR's Real Unsolved Problem in Gene Therapy
8+ hour, 1+ min ago (291+ words) No animal performs voluntary macroscopic body reshaping at human scale — but three biological systems provide the raw scientific ingredients that, in combination, describe what Clayface is doing: The freshwater polyp Hydra vulgaris is effectively biologically immortal, regenerating a complete organism…...
Sensorion Announces SENS-601 Program Day Focused on GJB2 Gene Therapy for Hearing Loss
8+ hour, 58+ min ago (225+ words) Sep 21, 2026 | Events, Research, Sensorineural | 0 | Sensorion, a clinical-stage biotechnology company focused on developing therapies to restore and treat hearing loss, has announced registration and connection details for its SENS-601 Program Day, scheduled for Sept 22, 2026. The event will be dedicated entirely to…...
Breaking barriers in brain gene therapy
8+ hour, 25+ min ago (979+ words) Researchers are now designing nanoparticles to navigate the brain and deliver genetic cargo to the right cells. During her postdoctoral training, however, she became increasingly interested in translating these technologies to real-world disease applications. Collaborations with clinicians working on traumatic…...
'Epigenetic' editing is here: gene-tagging technique banishes hepatitis B virus
8+ hour, 36+ min ago (211+ words) Technique uses chemical tags to shut down viral DNA lurking in host’s genome....
Base Editing Corrected TFG Mutation in Motor Neuron Disease
10+ hour, 24+ min ago (26+ words) Technology Networks Base editing rescues a hereditary motor neuron disease in mouse and patient-derived iPSC organoid models...
Suppressor tRNAs restore full-length dystrophin in mice with Duchenne muscular dystrophy
3+ day, 3+ hour ago (362+ words) Federation: Log in through a federation service that connects your organization to multiple systems. Use this option if your organization instructs you to use federated sign-in. Suppressor tRNAs restore full-length dystrophin in mice with Duchenne muscular dystrophy Roughly 15% of DMD…...